Columnist Betty Vertin's track career ended years ago, but she never stopped lifting weights — only now its the emotional weight of Duchenne.
New research shows DMD is marked by abnormalities in muscle development in the womb, supporting the potential of a therapy ...
The FDA updated prescribing information for Elevidys with new safety warnings and limiting its use to DMD patients who can ...
Columnist Shalom Lim reflects with gratitude on how he's found purpose by supporting other Singaporeans on their own health ...
Agamree is as effective as traditional corticosteroids at preserving walking ability but carries a lower risk of side effects ...
Columnist Robin Stemple and others in the Western Pennsylvania chapter of the FSHD Society raised $85,000 for research toward ...
When I was a young mom watching my oldest daughter, Lexi, move from upper elementary to middle school, I often felt heartbroken and helpless. She was an excellent student and friend at school, but ...
Whether it's transportation, education, or treatment, the more choices people with LGMD have, the better, says columnist.
Sarepta said DMD treatments Amondys 45 and Vyondys 53 show 'positive and encouraging trends' even though a trial failed to meet its main goal.
Histone deacetylase inhibitors are a treatment approach designed to work by blocking an enzyme that turns off gene activity. This may ultimately help by slowing muscle loss and disease progression.