Rare Disease Advisor, a trusted source of medical news and feature content for healthcare providers, offers clinicians insight into the latest research to inform clinical practice and improve patient ...

Generalized pustular psoriasis (GPP) is a rare, severe form of psoriasis characterized by the acute onset of eruptions of sterile pus-filled skin lesions and rashes with or without systemic ...

There was a reduction in volume of involvement, cardiac pyrophosphate activity, native T1, and extracellular volume during a median of 369 days between scans in patients with ATTR-CM being treated.

More than half (56.3%) of the patients with PBC treated with seladelpar as a second-line therapy achieved a biochemical response. The efficacy of seladelpar as a second-line therapy in patients with ...

The recommendations were based on the available evidence, its certainty, and key judgments using the Grading of Recommendations Assessment, Development and Evaluation framework. New guidelines ...

A single dose of efgartimod, rather than a 4-week regimen, was utilized prior to thymectomy, reducing the treatment cost and the decision-to-surgery time. Treatment with efgartigimod prior to ...